A Makeover For An Old Drug
Wilson disease (WD) was always fatal until Dr. John Walshe, an English physician, discovered penicillamine in 1956. While WD was no longer a death sentence, with time, complications with the drug [...]
The 100th Registry Participant
By Rhonda Rowland, WDA President I’m study participant number 30 in the Wilson Disease (WD) Patient Registry. That’s not exciting. However, if you’re participant number 100, you represent a milestone. And, that is [...]
Meet the Inaugural Gene Therapy Candidates
By Rhonda Rowland, WDA President The two gene therapy clinical trials for Wilson disease (WD) launched by Ultragenyx and Vivet Therapeutics are underway! Here, we introduce the WD community to two [...]